A new form of gene therapy has cured three bubble dogs. It lends hope that some day this may also be a treatment for humans.
The basset hounds had a rare disorder called XSCID. This disorder is known in humans as the bubble boy disorder. 1 in 100,000 boys receive a faulty gene from their mother. (It’s passed through the X chromosome.)
Dr. Felsburg, a professor of immunology at the University of Pennsylvania School of Veterinary Medicine, was in charge of the project. His team treated the dogs by injecting them with a corrected gene. These gene helps the immune system do it’s job.
XSCID is life threatening. At this time there is only one treatment for humans. While this new gene therapy is in it’s infancy and has only been used on dogs, in the future it could be another treatment for humans with the disorder.